Papillon Therapeutics

Papillon Therapeutics is a clinical-stage biotechnology company developing multi-systemic genetic medicines, including a gene-corrected hematopoietic stem cell therapy for Friedreich's ataxia that has received FDA Orphan Drug and Rare Pediatric Disease designations, evaluated for automated manufacturing with Cellares.

Company Facts

• Headquarters: San Diego, United States
• Type: startup
• Industries: Gene Therapy, Biopharmaceuticals, Rare Disease